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Biological Products. Prevention, Diagnosis, Treatment

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ISSUE TOPIC: DEVELOPMENT OF MEDICINAL PRODUCTS FOR THE TREATMENT OF RARE (ORPHAN) DISEASES

 
Issue Title
 
Vol 26, No 2 (2026) Development of acid alpha-glucosidase-producing clones based on the CHO-K1 cell line Abstract   PDF (Rus)
S. S. Timonova, S. S. Shubina, J. S. Snegireva, R. L. Anisimov, N. V. Nikiforova, D. A. Tretyak, M. A. Koroleva, M. Yu. Neronova, R. A. Khamitov
 
Vol 26, No 2 (2026) Tissue specificity and age-related dynamics of CAG promoter activity in rAAV-mediated gene therapy Abstract   PDF (Rus)
R. L. Anisimov, N. V. Nikiforova, E. S. Ivanov, A. A. Ovsepyan, A. A. Borzov, A. A. Kazarov
 
Vol 26, No 2 (2026) Evolution of therapy monogenic orphan diseases and regulatory aspects of orphan medicinal products development Abstract   PDF (Rus)
D. A. Poteryaev, R. A. Khamitov
 
Vol 26, No 2 (2026) Preclinical development of pediatric orphan gene therapy medicinal products: Analysis of approaches and challenges (review) Abstract   PDF (Rus)
A. M. Azarova, N. A. Gavrilova, M. V. Tikhomirova
 
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