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| Issue |
Title |
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| Vol 26, No 2 (2026) |
Development of acid alpha-glucosidase-producing clones based on the CHO-K1 cell line |
Abstract
PDF (Rus)
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S. S. Timonova, S. S. Shubina, J. S. Snegireva, R. L. Anisimov, N. V. Nikiforova, D. A. Tretyak, M. A. Koroleva, M. Yu. Neronova, R. A. Khamitov |
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| Vol 26, No 2 (2026) |
Tissue specificity and age-related dynamics of CAG promoter activity in rAAV-mediated gene therapy |
Abstract
PDF (Rus)
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R. L. Anisimov, N. V. Nikiforova, E. S. Ivanov, A. A. Ovsepyan, A. A. Borzov, A. A. Kazarov |
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| Vol 26, No 2 (2026) |
Evolution of therapy monogenic orphan diseases and regulatory aspects of orphan medicinal products development |
Abstract
PDF (Rus)
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D. A. Poteryaev, R. A. Khamitov |
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| Vol 26, No 2 (2026) |
Preclinical development of pediatric orphan gene therapy medicinal products: Analysis of approaches and challenges (review) |
Abstract
PDF (Rus)
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A. M. Azarova, N. A. Gavrilova, M. V. Tikhomirova |
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