For citations:

Azarova A.M., Gavrilova N.A., Tikhomirova M.V. Preclinical development of pediatric orphan gene therapy medicinal products: Analysis of approaches and challenges (review). Biological Products. Prevention, Diagnosis, Treatment. 2026;26(2):144-158. (In Russ.) https://doi.org/10.30895/2221-996X-2026-26-2-144-158